Type:

Other

Description:

Cartier et al. report another major advance—the successful first clinical testing of an HIV-derived vector in hematopoietic stem cell (HSC)–based gene therapy. The procedure was used to treat a severe neurodegenerative disease, X-linked adrenoleukodystrophy (ALD), and the results indicate stable expression of a therapeutic gene in a substantial fraction of patients' hematopoietic cells, as well as clinical benefits.

Subjects:

    Education Levels:

      Keywords:

      HSC,lentiviral vectors,hematopoietic stem cell,NSDL_SetSpec_BEN,HIV derived vector,gene therapy,oai:nsdl.org:2200/20110722022510061T,adrenoleukodystrophy,Life Science,(ALD),NSDL

      Language:

      English

      Access Privileges:

      Public - Available to anyone

      License Deed:

      Creative Commons Attribution Non-Commercial Share Alike

      Collections:

      None
      This resource has not yet been aligned.
      Curriki Rating
      'NR' - This resource has not been rated
      NR
      'NR' - This resource has not been rated

      This resource has not yet been reviewed.

      Not Rated Yet.

      Non-profit Tax ID # 203478467